WHAT ASRE TREATS
A Look at the Disorders We Focus On
Enzerna is focused on addressing three major nucleotide repeat-causing disorders. These three ASRE constructs will allow us to potentially address over 20 disorders caused by these repeats.
01
Myotonic Dystrophy
This type of muscular dystrophy is a genetic disorder that affects muscle function.
02
Huntington's Disease
Learn about how our therapeutic strategies can target Huntington’s Disease.