Diseases

The Conditions We Target

WHAT ASRE TREATS

A Look at the Disorders We Focus On

Enzerna is focused on addressing three major nucleotide repeat-causing disorders. These three ASRE constructs will allow us to potentially address over 20 disorders caused by these repeats.

Enzerna's graphic for ASRE and the disorders and diseases it targets.
01

Myotonic Dystrophy

This type of muscular dystrophy is a genetic disorder that affects muscle function. 

02

Huntington's Disease

Learn about how our therapeutic strategies can target Huntington’s Disease.

Scroll to top